biotech.quantcalc.app

Registered primary completions

Every active, company-sponsored Phase 3 in the cohort, by the primary completion date on its registry record. Registry dates are the sponsor's estimate and move.

Primary completion CompanyIndicationMarket capRunway (qtrs)
2026-09-01RGNXRegenxbio IncMucopolysaccharidosis Type II (MPS II)$638M2.5
2026-09-01ARDXArdelyx IncIrritable Bowel Syndrome With Constipati$984M20.5
2026-09-01VNDAVanda Pharmaceuticals IncSocial Anxiety Disorder (SAD)$320M9.5
2026-09-01IRONDisc Medicine IncErythropoietic Protoporphyria (EPP)$3,073M10.9
2026-09-01INCYIncyte CorpChronic Graft-versus-host-disease$25,210M
2026-09-01ALKSAlkermes PlcNarcolepsy Type 1$7,954M
2026-09-17VRTXVertex Pharmaceuticals IncBeta-Thalassemia$137,297M
2026-09-28OCGNOcugen IncStargardt Disease$448M6.1
2026-10-01BHVNBiohaven LtdFocal Epilepsy$2,328M1.7
2026-10-01CLDXCelldex Therapeutics IncChronic Inducible Urticaria$3,072M9.5
2026-10-01MIRMMirum Pharmaceuticals IncChronic Hepatitis D Infection$5,943M2.1
2026-10-01ABBVAbbvie IncAMD$451,463M
2026-10-07REGNRegeneron PharmaceuticalsAdvanced Non-Small Cell Lung Cancer$81,766M
2026-10-31OLMAOlema Pharmaceuticals IncBreast Cancer$899M8.4
2026-10-31ANNXAnnexon IncGeographic Atrophy$942M3.9
2026-10-31SRPTSarepta Therapeutics IncMuscular Dystrophy, Duchenne$2,203M
2026-10-31TGTXTg Therapeutics IncRelapsing Multiple Sclerosis$8,256M
2026-11-01CGONCg Oncology IncNon Muscle Invasive Bladder Cancer$6,590M16.3
2026-11-01SRRKScholar Rock Holding CorpSpinal Muscular Atrophy$7,039M4.6
2026-12-01CMPXCompass Therapeutics IncBiliary Tract Cancer$432M8.5
2026-12-01VIRVir Biotechnology IncViral Hepatitis$1,833M6.0
2026-12-01KRYSKrystal Biotech IncDystrophic Epidermolysis Bullosa$10,403M
2026-12-01IONSIonis Pharmaceuticals IncHereditary Angioedema (HAE)$10,146M13.8
2026-12-01MDGLMadrigal Pharmaceuticals IncNASH$12,332M10.8
2026-12-01UTHRUnited Therapeutics CorpIdiopathic Pulmonary Fibrosis$22,108M
2026-12-15EXELExelixis IncMetastatic Prostate Cancer$13,492M
2026-12-31INSMInsmed IncPulmonary Hypertension$25,887M2.6
2027-01-01PCVXVaxcyte IncPneumococcal Vaccines$8,904M5.3
2027-01-01BBIOBridgebio Pharma IncHypochondroplasia$14,975M5.6
2027-01-15IDYAIdeaya Biosciences IncUveal Melanoma$3,870M15.7
2027-02-01KODKodiak Sciences IncMacular Edema Secondary to Inflammation$2,371M2.1
2027-03-01STOKStoke Therapeutics IncDravet Syndrome$2,040M6.2
2027-03-13RYTMRhythm Pharmaceuticals IncHypothalamic Obesity$7,379M6.7
2027-05-01VORVor Biopharma IncPrimary Sjogren's Disease$1,340M2.0
2027-06-01SVRASavara IncAutoimmune Pulmonary Alveolar Proteinosi$1,081M4.9
2027-06-01DNLIDenali Therapeutics IncMucopolysaccharidosis II$3,836M5.3
2027-06-01GILDGilead Sciences IncTriple Negative Breast Cancer$180,637M10.8
2027-07-01NTLAIntellia Therapeutics IncNeuromuscular Disease$1,803M4.0
2027-07-01VKTXViking Therapeutics IncWeight Loss$3,752M4.3
2027-07-01NBIXNeurocrine Biosciences IncCongenital Adrenal Hyperplasia$15,660M
2027-08-01TVTXTravere Therapeutics IncHomocystinuria$6,190M56.8
2027-09-01CYTKCytokinetics IncPediatric$10,022M7.3
2027-11-01CRVSCorvus Pharmaceuticals IncPeripheral T-Cell Lymphoma, Not Otherwis$1,191M15.7
2027-12-01IMVTImmunovant IncGeneralized Myasthenia Gravis$8,510M
2027-12-01RVMDRevolution Medicines IncNSCLC$44,556M10.3
2027-12-27ALNYAlnylam Pharmaceuticals IncTransthyretin Amyloidosis With Cardiomyo$31,726M
2027-12-31PTCTPtc Therapeutics IncPhenylketonuria$5,850M
2028-01-01ACADAcadia Pharmaceuticals IncAlzheimer's Disease Psychosis$5,016M
2028-03-01ORICOric Pharmaceuticals IncMetastatic Castration Resistant Prostate$1,372M3.2
2028-03-01IOVAIovance Biotherapeutics IncMetastatic Melanoma$3,628M3.5
2028-03-01HALOHalozyme Therapeutics IncHypogonadism, Male$11,957M
2028-04-01RCUSArcus Biosciences IncMetastatic Pancreatic Ductal Adenocarcin$3,674M7.4
2028-04-01BCAXBicara Therapeutics IncMetastatic Head and Neck Squamous Cell C$1,550M8.6
2028-04-01SMMTSummit Therapeutics IncMetastatic Colorectal Cancer (CRC)$10,953M
2028-04-01ERASErasca IncAdvanced or Metastatic NRAS-mutant Melan$6,306M1.3
2028-04-30RLAYRelay Therapeutics IncPIK3CA Mutation$4,113M1.5
2028-06-30GERNGeron CorpMyelodysplastic Syndromes$970M40.4
2028-07-01CABACabaletta Bio IncSystemic Sclerosis$529M4.8
2028-07-01DYNDyne Therapeutics IncDuchenne Muscular Dystrophy (DMD)$4,682M6.7
2028-09-01IBRXImmunitybio IncBladder Cancer$8,532M5.5
2028-10-15VSTMVerastem IncLow Grade Serous Ovarian Cancer$654M3.8
2028-12-01DNTHDianthus Therapeutics IncMyasthenia Gravis, Generalized$5,920M19.4
2029-01-01SLDBSolid Biosciences IncDuchenne Muscular Dystrophy$1,048M7.4
2029-02-01AVBPArrivent Biopharma IncNon-Small-Cell Lung Cancer$1,488M8.7
2029-03-01AGIOAgios Pharmaceuticals IncPediatric Pyruvate Kinase Deficiency$1,989M5.3
2029-03-31CELCCelcuity IncBreast Cancer$4,328M14.8
2029-05-01INBXInhibrx Biosciences IncHead and Neck Squamous Cell Carcinoma (H$1,816M4.3
2029-06-01SNDXSyndax Pharmaceuticals IncAcute Myeloid Leukemias$1,745M10.9
2029-06-01BMRNBiomarin Pharmaceutical IncHemophilia A$12,517M
2030-01-01REPLReplimune Group IncAdvanced Melanoma$1,460M2.5
2030-02-01VCELVericel CorpChondral Defect$2,097M104.7
2030-06-01ZBIOZenas Biopharma IncMultiple Sclerosis (MS) Primary Progress$2,038M8.8
2031-06-01TSHATaysha Gene Therapies IncRett Syndrome$1,880M12.0
2031-08-01BCRXBiocryst Pharmaceuticals IncHereditary Angioedema$2,509M2.6
2031-10-22CADLCandel Therapeutics IncNon-squamous, Non-Small Cell Lung Cancer$1,000M12.0
2031-11-01KURAKura Oncology IncAcute Myeloid Leukemia (AML)$1,126M6.8